Product information and disease descriptionPlace of product in therapyApproaches to treatmentCurrent treatment options and standard of care
Exon-skipping antisense oligonucleotides
1 evidence topic · 1 source
Mutation-specific exon-skipping options
| Drug | Required exon-skipping amenability |
|---|---|
| Casimersen | “skipping exon 45.” |
| Viltolarsen | “skipping exon 53.” |
| Golodirsen | “skipping exon 53.” |
| Eteplirsen | “skipping exon 51.” |