Section 6 of 6
References
100 sources
- Balwani (2019) (opens in a new tab)
- Balwani and Desnick (2019) (opens in a new tab)
- Balwani et al. (2017a) (opens in a new tab)
- Balwani et al. (2017b) (opens in a new tab)
- Balwani et al. (2020) (opens in a new tab)
- Balwani et al. (2023) (opens in a new tab)
- Barman-Aksözen et al. (2020) (opens in a new tab)
- Barman-Aksözen et al. (2023a) (opens in a new tab)
- Barman-Aksözen et al. (2023b) (opens in a new tab)
- Barman-Aksözen et al. (2026) (opens in a new tab)
- Bell et al. (2026) (opens in a new tab)
- Belongie et al. (2022) (opens in a new tab)
- Biolcati et al. (2015) (opens in a new tab)
- ClinicalTrials.gov NCT03520036 (opens in a new tab)
- ClinicalTrials.gov NCT03520036 (opens in a new tab)
- ClinicalTrials.gov NCT04402489 (opens in a new tab)
- ClinicalTrials.gov NCT04402489 (opens in a new tab)
- ClinicalTrials.gov NCT05005975 (opens in a new tab)
- ClinicalTrials.gov NCT05020184 (opens in a new tab)
- ClinicalTrials.gov NCT06144840 (opens in a new tab)
- ClinicalTrials.gov NCT06910358 (opens in a new tab)
- ClinicalTrials.gov NCT06994286 (opens in a new tab)
- ClinicalTrials.gov NCT07820085 (opens in a new tab)
- Clinuvel Pharmaceuticals (2017) (opens in a new tab)
- Clinuvel Pharmaceuticals (2026) (opens in a new tab)
- Dechant et al. (2025) (opens in a new tab)
- DerSarkissian et al. (2025) (opens in a new tab)
- Di Pierro et al. (2022) (opens in a new tab)
- Dickey et al. (2021) (opens in a new tab)
- Dickey et al. (2023) (opens in a new tab)
- Disc Medicine (2026) (opens in a new tab)
- Disc Medicine (2026) (opens in a new tab)
- Elder et al. (2013) (opens in a new tab)
- EU Clinical Trials Register (2021) (opens in a new tab)
- EU Clinical Trials Register (2023) (opens in a new tab)
- European Medicines Agency (2022) (opens in a new tab)
- European Medicines Agency (2025) (opens in a new tab)
- Gemeinsamer Bundesausschuss (2021) (opens in a new tab)
- GondolaBio (2025) (opens in a new tab)
- GondolaBio (2026) (opens in a new tab)
- Graziadei et al. (2022) (opens in a new tab)
- Holme et al. (2006) (opens in a new tab)
- Horizonscan Geneesmiddelen (2026) (opens in a new tab)
- Jaramillo-Calle (2021) (opens in a new tab)
- jRCT2080225355 (opens in a new tab)
- Kluijver et al. (2024) (opens in a new tab)
- Kluijver et al. (2025) (opens in a new tab)
- Lala et al. (2018) (opens in a new tab)
- Langendonk et al. (2015) (opens in a new tab)
- LEO Pharma (2026) (opens in a new tab)
- LEO Pharma (2026) (opens in a new tab)
- Levy et al. (2024) (opens in a new tab)
- Levy et al. (2025) (opens in a new tab)
- Madigan et al. (2023) (opens in a new tab)
- Mathias et al. (2023) (opens in a new tab)
- McNamara (2026) (opens in a new tab)
- Minder et al. (2025) (opens in a new tab)
- Mitsubishi Tanabe Pharma America (2024) (opens in a new tab)
- Mitsubishi Tanabe Pharma Development America (2019) (opens in a new tab)
- Mitsubishi Tanabe Pharma Development America (2021) (opens in a new tab)
- Mitsubishi Tanabe Pharma Development America (2022) (opens in a new tab)
- Naik et al. (2019a) (opens in a new tab)
- Naik et al. (2019b) (opens in a new tab)
- Naik et al. (2025a) (opens in a new tab)
- Naik et al. (2025b) (opens in a new tab)
- Naik et al. (2025c) (opens in a new tab)
- NICE (2023) (opens in a new tab)
- NICE (2023) (opens in a new tab)
- NICE (2023) (opens in a new tab)
- NIHR Innovation Observatory (2022) (opens in a new tab)
- NORD (2022) (opens in a new tab)
- Norwegian Medicines Agency (2018) (opens in a new tab)
- Ogasawara et al. (2023) (opens in a new tab)
- Ogasawara et al. (2024) (opens in a new tab)
- Ogasawara et al. (2025a) (opens in a new tab)
- Ogasawara et al. (2025b) (opens in a new tab)
- Ogawa et al. (2023) (opens in a new tab)
- Raef et al. (2023) (opens in a new tab)
- Ross et al. (2026) (opens in a new tab)
- Sato et al. (2024) (opens in a new tab)
- Silver et al. (2025) (opens in a new tab)
- Suzuki et al. (2022) (opens in a new tab)
- Tanabe Pharma America (2024) (opens in a new tab)
- Tanabe Pharma America (2025) (opens in a new tab)
- Tanabe Pharma America (2026) (opens in a new tab)
- Tanabe Pharma Corporation (2025) (opens in a new tab)
- Tanabe Pharma Corporation (2026) (opens in a new tab)
- Tanabe Pharma Corporation (2026) (opens in a new tab)
- Tanabe Pharma Corporation (2026) (opens in a new tab)
- Thompson et al. (2016) (opens in a new tab)
- Tran et al. (2025) (opens in a new tab)
- Tsuda et al. (2023) (opens in a new tab)
- US Food and Drug Administration (2019) (opens in a new tab)
- Ventura et al. (2020) (opens in a new tab)
- Wensink et al. (2020) (opens in a new tab)
- Wensink et al. (2021) (opens in a new tab)
- Wensink et al. (2022) (opens in a new tab)
- Wensink et al. (2023) (opens in a new tab)
- Whatley et al. (2010) (opens in a new tab)
- Yeung et al. (2026) (opens in a new tab)