Section 6 of 6
References
155 sources
- Alshammari et al. (2026) (opens in a new tab)
- Amayiri et al. (2024) (opens in a new tab)
- Armstrong et al. (2009) (opens in a new tab)
- Armstrong et al. (2011) (opens in a new tab)
- ASHP AHFS DI Essentials tovorafenib monograph (2025) (opens in a new tab)
- Ater et al. (2012) (opens in a new tab)
- Avery and Hardy (2014) (opens in a new tab)
- Bandopadhayay et al. (2014) (opens in a new tab)
- Barbato et al. (2024) (opens in a new tab)
- Bates et al. (2022) (opens in a new tab)
- Bazer et al. (2026) (opens in a new tab)
- Bennebroek et al. (2025) (opens in a new tab)
- Blue Cross Blue Shield Association FEP medical policy 5.21.222 (2025) (opens in a new tab)
- Bouffet et al. (2023a) (opens in a new tab)
- Bouffet et al. (2023b) (opens in a new tab)
- Brizini et al. (2026) (opens in a new tab)
- Buhl et al. (2019) (opens in a new tab)
- CDA-AMC dabrafenib plus trametinib reimbursement review (2025) (opens in a new tab)
- Cherlow et al. (2019) (opens in a new tab)
- Chugai Pharmaceutical companion diagnostic announcement (2026) (opens in a new tab)
- ClinicalTrials.gov NCT01425008 (opens in a new tab)
- ClinicalTrials.gov NCT03429803 (opens in a new tab)
- ClinicalTrials.gov NCT03871257 (opens in a new tab)
- ClinicalTrials.gov NCT04166409 (opens in a new tab)
- ClinicalTrials.gov NCT05566795 (opens in a new tab)
- CMS advanced diagnostic laboratory tests list (2025) (opens in a new tab)
- Crotty et al. (2025) (opens in a new tab)
- DailyMed OJEMDA prescribing information (2025) (opens in a new tab)
- Damodharan et al. (2026) (opens in a new tab)
- Day One Biopharmaceuticals accelerated approval announcement (2024) (opens in a new tab)
- Day One Biopharmaceuticals and Servier FIREFLY-2 enrollment announcement (2026) (opens in a new tab)
- Day One Biopharmaceuticals and Servier FIREFLY-2 enrollment announcement (2026) (opens in a new tab)
- Day One Biopharmaceuticals Connecticut prescriber price disclosure (2025) (opens in a new tab)
- Day One Biopharmaceuticals EveryDay Support HCP support team page (opens in a new tab)
- Day One Biopharmaceuticals Form 10-K (2026) (opens in a new tab)
- Day One Biopharmaceuticals fourth quarter 2025 results (2026) (opens in a new tab)
- Day One Biopharmaceuticals OJEMDA support page (opens in a new tab)
- Day One Biopharmaceuticals preliminary 2025 revenue announcement (2026) (opens in a new tab)
- Day One Biopharmaceuticals Schedule 14D-9 (2026) (opens in a new tab)
- Day One Biopharmaceuticals Series A announcement (2020) (opens in a new tab)
- de Blank et al. (2016) (opens in a new tab)
- de Blank et al. (2017) (opens in a new tab)
- de Bont and Schouten-van Meeteren (2024) (opens in a new tab)
- Dodgshun et al. (2016) (opens in a new tab)
- EMA Ojemda medicine overview (2026) (opens in a new tab)
- EMA Ojemda product information (2026) (opens in a new tab)
- EMA Ojemda public assessment report (2026) (opens in a new tab)
- Embring et al. (2026) (opens in a new tab)
- Erker et al. (2024) (opens in a new tab)
- Falzon et al. (2018) (opens in a new tab)
- Fangusaro et al. (2019) (opens in a new tab)
- Fangusaro et al. (2021) (opens in a new tab)
- Fangusaro et al. (2024) (opens in a new tab)
- Fangusaro et al. (2025) (opens in a new tab)
- Farias de Alvarenga et al. (2026) (opens in a new tab)
- FDA accelerated approval announcement (2024) (opens in a new tab)
- FDA approval letter NDA 217700 (2024) (opens in a new tab)
- FDA multi-discipline review NDA 217700 and 218033 (2024) (opens in a new tab)
- FDA Ongoing Cancer Accelerated Approvals (2026) (opens in a new tab)
- FDA risk assessment and risk mitigation review NDA 217700 and 218033 (2024) (opens in a new tab)
- FDA supplement approval letter NDA 217700 (2025) (opens in a new tab)
- Figueira and Pigott (2026) (opens in a new tab)
- Fisher et al. (2012) (opens in a new tab)
- Forbrigger et al. (2026) (opens in a new tab)
- Foundation Medicine (2025) (opens in a new tab)
- G-BA benefit assessment procedure tovorafenib (2026) (opens in a new tab)
- G-BA Nutzenbewertung tovorafenib (2026) (opens in a new tab)
- Gajjar et al. (2025) (opens in a new tab)
- Gascon et al. (2024) (opens in a new tab)
- Gascon et al. (2026) (opens in a new tab)
- Giantini-Larsen et al. (2025) (opens in a new tab)
- Gnekow et al. (2012) (opens in a new tab)
- Gnekow et al. (2017) (opens in a new tab)
- Gnekow et al. (2019) (opens in a new tab)
- Grin et al. (2026) (opens in a new tab)
- Hammad et al. (2024) (opens in a new tab)
- Hanania et al. (2021) (opens in a new tab)
- Hargrave et al. (2026) (opens in a new tab)
- HAS OJEMDA early access decision (2026) (opens in a new tab)
- HTACG tovorafenib JCA report (2026) (opens in a new tab)
- HTACG tovorafenib JCA summary report (2026) (opens in a new tab)
- ICER Launch Price and Access Report (2025) (opens in a new tab)
- Ipsen and Day One Biopharmaceuticals licensing announcement (2024) (opens in a new tab)
- Ipsen EU approval announcement (2026) (opens in a new tab)
- Ipsen H1 2026 results (2026) (opens in a new tab)
- IPSEN Japan approval announcement (2026) (opens in a new tab)
- Ipsen Joint Clinical Assessment publication update (2026) (opens in a new tab)
- IQWiG dossier assessment G26-11 (2026) (opens in a new tab)
- IQWiG G26-11 project page (2026) (opens in a new tab)
- Jacob et al. (2011) (opens in a new tab)
- Jalal et al. (2025) (opens in a new tab)
- Jones et al. (2008) (opens in a new tab)
- Jones et al. (2013) (opens in a new tab)
- Kelada et al. (2020) (opens in a new tab)
- Khuong Quang et al. (2026) (opens in a new tab)
- Kilburn et al. (2024) (opens in a new tab)
- Kline et al. (2024a) (opens in a new tab)
- Kline et al. (2024b) (opens in a new tab)
- Kline et al. (2025) (opens in a new tab)
- Kline et al. (2026a) (opens in a new tab)
- Kline et al. (2026b) (opens in a new tab)
- Krishnatry et al. (2016) (opens in a new tab)
- Lafay-Cousin et al. (2008) (opens in a new tab)
- Lassaletta et al. (2016) (opens in a new tab)
- Lassaletta et al. (2017) (opens in a new tab)
- Lassaletta et al. (2024) (opens in a new tab)
- Louis et al. (2021) (opens in a new tab)
- Merchant et al. (2009) (opens in a new tab)
- Miser et al. (2023) (opens in a new tab)
- Musial-Bright et al. (2011) (opens in a new tab)
- NCCN Guidelines Pediatric Central Nervous System Cancers (opens in a new tab)
- NICE ID6557 project information (2025) (opens in a new tab)
- NICE TA977 (2024) (opens in a new tab)
- Nobre et al. (2020) (opens in a new tab)
- Nwachukwu et al. (2015) (opens in a new tab)
- Nysom et al. (2025) (opens in a new tab)
- O'Hare et al. (2024) (opens in a new tab)
- Peipert et al. (2024) (opens in a new tab)
- Perreault et al. (2019) (opens in a new tab)
- Pharma Japan (2026) (opens in a new tab)
- Picariello et al. (2026) (opens in a new tab)
- Price et al. (2025) (opens in a new tab)
- Raabe et al. (2011) (opens in a new tab)
- Rafia et al. (2026) (opens in a new tab)
- Ramagopalan and Pannelay (2026) (opens in a new tab)
- Rasco et al. (2023) (opens in a new tab)
- Rios et al. (2022) (opens in a new tab)
- Rocque et al. (2019) (opens in a new tab)
- Roka et al. (2024) (opens in a new tab)
- Roser et al. (2019) (opens in a new tab)
- Ruggiero et al. (2026) (opens in a new tab)
- Ryall et al. (2020a) (opens in a new tab)
- Ryall et al. (2020b) (opens in a new tab)
- Servier (2026) (opens in a new tab)
- Servier acquisition completion announcement (2026) (opens in a new tab)
- Singh et al. (2025) (opens in a new tab)
- SIOPE Brain Tumour Group standard clinical practice recommendations (2022) (opens in a new tab)
- Stiller et al. (2019) (opens in a new tab)
- Stokland et al. (2010) (opens in a new tab)
- Sturm et al. (2023) (opens in a new tab)
- Styczewska et al. (2026) (opens in a new tab)
- Sun et al. (2017) (opens in a new tab)
- Tkacik et al. (2023) (opens in a new tab)
- Tsang et al. (2017) (opens in a new tab)
- Tsimicalis et al. (2011) (opens in a new tab)
- van Tilburg et al. (2024) (opens in a new tab)
- Warner et al. (2015) (opens in a new tab)
- Wen et al. (2022) (opens in a new tab)
- Williams et al. (2018) (opens in a new tab)
- Wilne et al. (2007) (opens in a new tab)
- Witt et al. (2025) (opens in a new tab)
- Wright et al. (2026) (opens in a new tab)
- Xu et al. (2026) (opens in a new tab)
- Zelt et al. (2024) (opens in a new tab)
- Zheng et al. (2026) (opens in a new tab)