Section 6 of 6
References
89 sources
- Akasaka et al. (2015) (opens in a new tab)
- Alfaro et al. (2025) (opens in a new tab)
- Alfaro et al. (2025) (opens in a new tab)
- Ataya et al. (2025a) (opens in a new tab)
- Ataya et al. (2025a) (opens in a new tab)
- Ataya et al. (2025b) (opens in a new tab)
- Bonella and Borie (2025a) (opens in a new tab)
- Bonella et al. (2025b) (opens in a new tab)
- Bonella et al. (2025c) (opens in a new tab)
- Campo et al. (2022) (opens in a new tab)
- Campo et al. (2024) (opens in a new tab)
- Carey et al. (2022) (opens in a new tab)
- CenterWatch (2026) (opens in a new tab)
- Chen et al. (2025a) (opens in a new tab)
- Chen et al. (2025b) (opens in a new tab)
- ClinicalTrials.gov NCT03482752 (opens in a new tab)
- ClinicalTrials.gov NCT04544293 (opens in a new tab)
- ClinicalTrials.gov NCT04544293 (opens in a new tab)
- ClinicalTrials.gov NCT06431776 (opens in a new tab)
- ClinicalTrials.gov NCT06546098 (opens in a new tab)
- CTIS.eu 2024-512039-66-00 (opens in a new tab)
- Dang et al. (2026) (opens in a new tab)
- European Respiratory Society (opens in a new tab)
- FDA Orphan Drug Designations and Approvals (2012) (opens in a new tab)
- Futami et al. (2026) (opens in a new tab)
- Gajewska et al. (2018) (opens in a new tab)
- Guirriec et al. (2024) (opens in a new tab)
- Higgins et al. (2026) (opens in a new tab)
- Inoue et al. (2008) (opens in a new tab)
- Inoue et al. (2008) (opens in a new tab)
- Inoue et al. (2026) (opens in a new tab)
- Jehn and Bonella (2023) (opens in a new tab)
- Jouneau et al. (2025) (opens in a new tab)
- Kavuru et al. (2011) (opens in a new tab)
- Kim et al. (2022) (opens in a new tab)
- Lee et al. (2025) (opens in a new tab)
- Lettieri et al. (2024) (opens in a new tab)
- Loyola Medicine (opens in a new tab)
- Luisetti et al. (2011) (opens in a new tab)
- Mabo et al. (2023) (opens in a new tab)
- McCarthy et al. (2018) (opens in a new tab)
- McCarthy et al. (2022) (opens in a new tab)
- McCarthy et al. (2025) (opens in a new tab)
- McCarthy et al. (2026a) (opens in a new tab)
- McCarthy et al. (2026b) (opens in a new tab)
- Montaño et al. (2025) (opens in a new tab)
- Munsif et al. (2023) (opens in a new tab)
- Naeem et al. (2026) (opens in a new tab)
- Narita et al. (2026) (opens in a new tab)
- National Health Care Institute Horizonscan Geneesmiddelen (2026) (opens in a new tab)
- Papiris et al. (2014) (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (opens in a new tab)
- Savara Inc. (2024) (opens in a new tab)
- Savara Inc. (2025) (opens in a new tab)
- Savara Inc. (2025) (opens in a new tab)
- Savara Inc. (2025) (opens in a new tab)
- Savara Inc. (2025) (opens in a new tab)
- Savara Inc. (2026) (opens in a new tab)
- Savara Inc. (2026) (opens in a new tab)
- Savara Inc. (2026) (opens in a new tab)
- Savara Inc. (2026) (opens in a new tab)
- Savara Inc. (2026) (opens in a new tab)
- Savara Inc. ERS presentation (2019) (opens in a new tab)
- Savara Inc. expanded access policy (opens in a new tab)
- Savara Inc. Form 10-K (2023) (opens in a new tab)
- Sheng et al. (2018) (opens in a new tab)
- Soyez et al. (2018) (opens in a new tab)
- Strong et al. (2025) (opens in a new tab)
- Tazawa et al. (2019) (opens in a new tab)
- Tian et al. (2020) (opens in a new tab)
- Trapnell (2024a) (opens in a new tab)
- Trapnell (2024a) (opens in a new tab)
- Trapnell et al. (2019) (opens in a new tab)
- Trapnell et al. (2020) (opens in a new tab)
- Trapnell et al. (2024b) (opens in a new tab)
- Trapnell et al. (2025a) (opens in a new tab)
- Trapnell et al. (2025b) (opens in a new tab)
- Trapnell et al. (2025b) (opens in a new tab)
- Trapnell et al. (2026) (opens in a new tab)
- Wang et al. (2025) (opens in a new tab)
- WHO Collaborating Centre for Drug Statistics Methodology (2026) (opens in a new tab)
- Xiong et al. (2026) (opens in a new tab)